9th June 2022

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Press Releases

FDA Advisory Committee Unanimously Endorses eli-cel Gene Therapy for Cerebral Adrenoleukodystrophy

Research study: Lorem ipsum dolor sit amet, per appetere percipit disputationi et, homero nostrud vituperatoribus in duo, id pro tota nobis.

18th May 2022

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Press Releases

SwanBio Therapeutics Announces $56 Million Series B Financing to Advance Novel Gene Therapies for Neurological Conditions

New funding will support ongoing clinical development of lead candidate, SBT101 for adrenomyeloneuropathy (AMN). New funding will support ongoing clinical...

17th May 2022

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Press Releases

Poxel Announces PXL065 and PXL770 Granted Orphan Drug Designation from the U.S. FDA for X-Linked Adrenoleukodystrophy

Poxel Announces PXL065 and PXL770 Granted Orphan Drug Designation from the U.S. FDA for X-Linked Adrenoleukodystrophy LYON, France–(BUSINESS WIRE)– POXEL SA (Euronext: POXEL – FR0012432516), a clinical stage biopharmaceutical company developing innovative … Continued

5th May 2022

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Natalie Grant presents at 2022 AAN Meeting

Natalie Grant presents at 2022 AAN Meeting Natalie Grant, Clinical Research Coordinator, at Massachusetts General Hospital presented, “Neurological Disease Burden in Females with X-Linked Adrenoleukodystrophy” at the 2022 American Academy … Continued

30th April 2022

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Dr. Jonanlis Ramirez Alcantara presents at the 2022 Pediatric Endocrine Society Meeting

Dr. Jonanlis Ramirez Alcantara presents at the 2022 Pediatric Endocrine Society Meeting Dr. Jonanlis Ramirez Alcantara, Clinical and Research Fellow at Massachusetts General Hospital, presented, “ADRENAL INSUFFICIENCY IN PEDIATRIC PATIENTS … Continued

14th April 2022

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Cellular, Tissue and Gene Therapies Advisory Committee; Notice of Meeting; Establishment of a Public Docket; Request for Comments

Cellular, Tissue and Gene Therapies Advisory Committee; Notice of Meeting; Establishment of a Public Docket; Request for Comments Original post by the Food and Drug Administration on Apr 13, 2022 The Food … Continued

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Raising awareness for adrenoleukodystrophy is essential to driving progress in research, support, and advocacy for the ALD community. By sharing information and spreading the word, you help amplify the voices of those affected and bring attention to the urgent need for improved care and scientific advancements.

News & Events

FDA Advisory Committee Unanimously Endorses eli-cel Gene Therapy for Cerebral Adrenoleukodystrophy

SwanBio Therapeutics Announces $56 Million Series B Financing to Advance Novel Gene Therapies for Neurological Conditions

Poxel Announces PXL065 and PXL770 Granted Orphan Drug Designation from the U.S. FDA for X-Linked Adrenoleukodystrophy

Natalie Grant presents at 2022 AAN Meeting

Dr. Jonanlis Ramirez Alcantara presents at the 2022 Pediatric Endocrine Society Meeting

Cellular, Tissue and Gene Therapies Advisory Committee; Notice of Meeting; Establishment of a Public Docket; Request for Comments

Raise Awareness for ALD

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