ALD Connect

ALD Connect Annual Meeting & Patient Learning Academy 2025

View video recordings from the 2025 ALD Connect Annual Meeting & Patient Learning Academy, which took place November 7–8, 2025, in Cambridge, Massachusetts.

ALD Connect Annual General Meeting 2025

Building the Future for ALD: Paradigm Shifts and Therapeutic Opportunities
Florian Eichler, MD
Characterization of Cholesterol Pathways in ALD Pathophysiology
Josh Bonkowsky, MD, PhD
The Grey Zone Project Risk-Based Classification of ABCD1 Variants in X-linked Adrenoleukodystrophy
Stephan Kemp, PhD
Two Tales to Tell: Gene Therapy 2.0 and Anti-MLC
Dr. Troy Lund, MD PhD MSMS FAAP
International Study of Meaningfulness of Sway and Gait to Assess AMN Sensorimotor Progression
Amena Smith Fine, MD PhD
Eda Kabak, MD
Patient Panel
2025 ALD Connect Awards
Gene Therapy Vectors
David A. Williams, MD
2024 ALD Connect Emerging Investigators
Maria L. Seixas
Nicki F. Coveña
Genotype Classification and C26-LPC Levels Predict ALD Symptoms in Boys Identified via NBS
Cecilie Videbaek, MD
Keith Van Haren, MD
Novel Brain Iron Imaging
Christina Nemeth Mertz, PhD
Eric Mallack, MD
CRISPR/Cas9 and Screening for the Levels of ABCD Transporters
Triana Amen, PhD
Minoryx Therapeutics: A Clinical Development Update
Arun Mistry, MBChB MRCP
Gene Editing Approaches
David Rufino Ramos, PhD

ALD Connect Patient Learning Academy 2025

Welcome to the Patient Learning Academy
ALD Connect Collaborative Research Network Update
Felicity Emerson, PhD
Fireside Chat: The Evolving ALD Landscape and Therapy Development
Ask the Experts
Closing Remarks

Useful Links

Annual Meeting and Patient Learning Academy
Annual Meeting and Patient Learning Academy
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ALD Connect Annual Meeting & Patient Learning Academy 2023